Arrakis Therapeutics Email Format
Pharmaceutical ManufacturingMassachusetts, United States51-200 Employees
Arrakis Therapeutics is a mid-sized biopharmaceutical company based in Waltham, Massachusetts. It focuses on expanding the reach of small-molecule medicines by directly modulating RNA, applying a drug-discovery framework traditionally used for protein targets to RNA biology. The firm aims to unlock RNA biology for medicine by pursuing targets that have been difficult to address with conventional approaches, broadening the range of biological processes that can be treated with small molecules. This work is guided by a mission to translate RNA biology into new therapeutic options for patients. Its target market comprises researchers and industry collaborators seeking RNA-targeted therapeutics to address diseases with unmet medical needs. In March 2025, Arrakis participated in the MDA Conference 2025, presenting an RNA-targeted small molecule intended to treat Myotonic Dystrophy.