Design Therapeutics Email Format
Biotechnology ResearchCalifornia, United States51-200 Employees
Design Therapeutics is a clinical-stage biotechnology company based in Carlsbad, California, focused on therapies that regulate the expression of disease-causing genes to address underlying causes of degenerative conditions. Its approach aims to adjust gene activity in order to influence disease progression for patients with genetic diseases, rather than simply treat symptoms. The lead program targets Friedreich ataxia, with additional efforts in Fuchs endothelial corneal dystrophy and myotonic dystrophy type-1, plus discovery work on other nucleotide-repeat-related disorders. As a mid-sized company in the biotechnology research sector, it pursues these therapies from its Carlsbad base. In 2026, management announced participation in a fireside chat at the Jefferies Global Healthcare Conference.
1-888-653-2347 
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