Cure Sanfilippo Foundation
Non-profit OrganizationsSouth Carolina, United States2-10 Employees
Cure Sanfilippo Foundation is a small nonprofit based in Columbia, South Carolina, focusing on advocacy and funding research toward a cure or effective treatments for Sanfilippo Syndrome in children. It serves families affected by the condition and researchers pursuing therapies, aiming to address the absence of approved treatments for a rapidly degenerative, fatal disease. Operating in the nonprofit sector of rare diseases, it positions itself at the intersection of patient advocacy and scientific funding. A notable development in its activities is a partnership formed in 2020 with RDMD to advance Sanfilippo research. The foundation concentrates on supporting research translation and policy advocacy to help move potential therapies toward clinical use.