Ascidian Therapeutics
Biotechnology ResearchMassachusetts, United States11-50 Employees
Ascidian Therapeutics is a biotechnology company based in Boston, Massachusetts. It aims to redefine disease treatment by rewriting RNA, editing exons at the RNA level to enable post-transcriptional changes that produce full-length, functional proteins in the right cells at the right time. Its discovery and preclinical programs target ophthalmology, neurology and neuromuscular disorders, and other rare diseases. Operating as a small to mid-sized firm in the biotechnology research sector, Ascidian collaborates with larger pharmaceutical companies to advance its RNA exon-editing approach. In June 2026, it announced a research collaboration with Eli Lilly to develop RNA exon editors for inherited kidney diseases.